Research

Life Sciences & Biotechnology

Title :

Small molecule oral agonist of the glucagon-like-peptide-1 receptor to improve glycemic control and nonalcoholic fatty liver disease in diabetes mellitus

Area of research :

Life Sciences & Biotechnology

Principal Investigator :

Dr. Prosenjit Mondal, Indian Institute Of Technology (IIT) Mandi, Himachal Pradesh

Timeline Start Year :

2023

Timeline End Year :

2026

Contact info :

Details

Executive Summary :

Pancreatic ? cell mass and function are compromised in both Type 1 Diabetes Mellitus (T1DM) and Type 2 Diabetes Mellitus (T2DM), with insulin resistance being a significant pathogenic factor in T2DM. This proposal aims to develop a small molecule that can protect and restore functional ?-cell mass to combat diabetes. The team designed and synthesized a series of small molecule GLP1R agonists, testing the top three compounds for their effect on maintaining or restoring functional ?-cell mass. One compound, PK2, displays stable binding with GLP1R, induces GLP1R internalization, and increases cAMP levels. PK2 also increases insulin secretion in vitro and protects against diabetes induced by multiple low-dose streptozotocin administration by lowering high blood glucose levels. Treatment of PK2 induces ?-cell replication and attenuates ?-cell apoptosis in STZ-treated mice. The central hypothesis is that PK2 is an orally active, non-peptide GLP-1R agonist that will preserve or restore functional ?-cell mass following ?-cell injury and replicates several important properties of native GLP-1 to combat diabetes. Preliminary data provides a strong position to test this hypothesis. The lead molecule PK2 will be explored in a HFD-induced NAFLD model, assessing its effect on body weight gain, food intake, energy expenditure, glucose intolerance, insulin resistance, and ?-cell dysfunction in diabetic mice. Further studies will provide deeper insight into PK2's mechanism of action.

Co-PI:

Dr. Bikash Medhi, Post Graduate Institute Of Medical Education And Research (PGIMER), Chandigarh-160012

Total Budget (INR):

56,98,870

Organizations involved